Gross Motor Function in Pediatric Onset TUBB4A-Related Leukodystrophy: GMFM-88 Performance and Validation of GMFC-MLD in TUBB4A

Francesco Gavazzi*, Virali Patel, Brittany Charsar, Allan Glanzman, Jacqueline Erler, Anjana Sevagamoorthy, Emma McKenzie, Tracy Kornafel, Elizabeth Ballance, Samuel R. Pierce, Michelle Teng, Brielle Formanowski, Sarah Woidill, Justine Shults, Evangeline Wassmer, Davide Tonduti, Francesca Magrinelli, Geneviève Bernard, Marjo Van Der Knaap, Nicole WolfLaura Adang, Adeline Vanderver

*Corresponding author for this work

Research output: Contribution to journalArticlepeer-review

Fingerprint

Dive into the research topics of 'Gross Motor Function in Pediatric Onset TUBB4A-Related Leukodystrophy: GMFM-88 Performance and Validation of GMFC-MLD in TUBB4A'. Together they form a unique fingerprint.

Medicine & Life Sciences